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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
1	1 Novartis NVS $279B	1,007	+69	+7%	$21.1B
2	2 Charles River Laboratories CRL $14.4B	339	+3	+0.9%	$5.16B
3	3 DELISTED bluebird bio BLUE	296	+53	+22%	$9.29B
4	4 DELISTED CATALENT, INC. CTLT	276	-10	-3%	$5.48B
5	5 Sarepta Therapeutics SRPT $1.78B	254	+21	+9%	$3.07B
6	6 DELISTED SANGAMO THERAPEUTICS INC SGMO	170	+22	+15%	$916M
7	7 Precigen PGEN $2.64B	163	+8	+5%	$1.13B
8	8 Ultragenyx Pharmaceutical RARE $1.47B	163	+9	+6%	$2.01B
9	9 PTC Therapeutics PTCT $4.98B	125	-4	-3%	$636M
10	10 Lineage Cell Therapeutics LCTX $232M	117	+15	+15%	$125M
11	11 Intellia Therapeutics NTLA $1.6B	112	+27	+32%	$467M
12	12 Regenxbio RGNX $454M	108	+19	+21%	$718M
13	ATHX 13 DELISTED Athersys, Inc. Common Stock ATHX	105	+8	+8%	$43.9M
14	SIOX 14 DELISTED Sio Gene Therapies Inc. Common Stock SIOX	105	-9	-8%	$528M
15	15 Voyager Therapeutics VYGR $124M	98	+23	+31%	$418M
16	16 Abeona Therapeutics ABEO $249M	93	+18	+24%	$464M
17	BLCM 17 DELISTED Bellicum Pharmaceuticals, Inc. BLCM	91	+3	+3%	$154M
18	18 Atara Biotherapeutics ATRA $96M	86	+4	+5%	$542M
19	19 CRISPR Therapeutics CRSP $4.86B	83	+19	+30%	$293M
20	20 Fate Therapeutics FATE $232M	78	+4	+5%	$216M
21	21 Lakefront Biotherapeutics American Depositary Shares LKFT $1.93B	77	+8	+12%	$932M
22	ISEE 22 DELISTED IVERIC bio, Inc. Common Stock ISEE	75	+8	+12%	$68.1M
23	ADAP 23 DELISTED Adaptimmune Therapeutics ADAP	71	+4	+6%	$348M
24	24 DELISTED Adverum Biotechnologies ADVM	65	+7	+12%	$67.3M
25	25 Cartesian Therapeutics RNAC $192M	63	+10	+19%	$107M