← All themes Genomics & Gene Editing

Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
1	1 Novartis NVS $279B	1,013	+6	+0.6%	$20.7B
2	2 Charles River Laboratories CRL $14.4B	333	-6	-2%	$5.03B
3	3 DELISTED bluebird bio BLUE	303	+7	+2%	$9B
4	4 DELISTED CATALENT, INC. CTLT	274	-2	-0.7%	$5.55B
5	5 Sarepta Therapeutics SRPT $1.78B	269	+15	+6%	$4.2B
6	6 DELISTED SANGAMO THERAPEUTICS INC SGMO	208	+38	+22%	$1.09B
7	7 Precigen PGEN $2.64B	166	+3	+2%	$1.66B
8	8 Ultragenyx Pharmaceutical RARE $1.47B	165	+2	+1%	$2.5B
9	9 PTC Therapeutics PTCT $4.98B	148	+23	+18%	$1.15B
10	10 CRISPR Therapeutics CRSP $4.86B	135	+52	+63%	$855M
11	11 Intellia Therapeutics NTLA $1.6B	130	+18	+16%	$557M
12	12 Regenxbio RGNX $454M	120	+12	+11%	$668M
13	13 Lineage Cell Therapeutics LCTX $232M	115	-2	-2%	$152M
14	14 Atara Biotherapeutics ATRA $96M	114	+28	+33%	$1.7B
15	15 Voyager Therapeutics VYGR $124M	108	+10	+10%	$509M
16	16 DELISTED Adverum Biotechnologies ADVM	96	+31	+48%	$201M
17	ATHX 17 DELISTED Athersys, Inc. Common Stock ATHX	94	-11	-10%	$42.6M
18	BLCM 18 DELISTED Bellicum Pharmaceuticals, Inc. BLCM	90	-1	-1%	$121M
19	19 Fate Therapeutics FATE $232M	90	+12	+15%	$385M
20	20 Abeona Therapeutics ABEO $249M	88	-5	-5%	$471M
21	21 Vericel Corp VCEL $2.06B	84	+34	+68%	$206M
22	22 Lakefront Biotherapeutics American Depositary Shares LKFT $1.93B	82	+5	+6%	$894M
23	SIOX 23 DELISTED Sio Gene Therapies Inc. Common Stock SIOX	81	-24	-23%	$19.7M
24	ADAP 24 DELISTED Adaptimmune Therapeutics ADAP	76	+5	+7%	$631M
25	ISEE 25 DELISTED IVERIC bio, Inc. Common Stock ISEE	71	-4	-5%	$58.3M