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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
MRKR icon
51
Marker Therapeutics
MRKR
$17.7M
60 +2 +3% $20.4M
LOGC
52
DELISTED
LogicBio Therapeutics, Inc. Common Stock
LOGC
59 +8 +16% $133M
CARM icon
53
DELISTED
Carisma Therapeutics
CARM
56 +11 +24% $37.3M
GMDA
54
DELISTED
Gamida Cell Ltd. Ordinary Shares
GMDA
56 +18 +47% $230M
PSTX icon
55
DELISTED
Poseida Therapeutics, Inc. Common Stock
PSTX
56 +4 +8% $288M
CABA icon
56
Cabaletta Bio
CABA
$242M
55 +1 +2% $202M
MESO icon
57
Mesoblast
MESO
$1.72B
53 +2 +4% $24.3M
FDMT icon
58
4D Molecular Therapeutics
FDMT
$682M
52 +52 – $602M
TSHA icon
59
Taysha Gene Therapies
TSHA
$1.18B
51 +5 +11% $475M
AUTL icon
60
Autolus Therapeutics
AUTL
$429M
48 +2 +4% $113M
PLUR icon
61
Pluri
PLUR
$12.2M
46 -6 -12% $37.7M
PTE
62
DELISTED
PolarityTE, Inc. Common Stock
PTE
46 +5 +12% $6.32M
SGTX
63
DELISTED
Sigilon Therapeutics, Inc. Common Stock
SGTX
45 +45 – $942M
ACET icon
64
Adicet Bio
ACET
$44M
44 +12 +38% $134M
OCGN icon
65
Ocugen
OCGN
$271M
43 +24 +126% $26.6M
IMTX icon
66
Immatics
IMTX
$1.04B
41 -3 -7% $216M
LNAI icon
67
Lunai Bioworks
LNAI
$3.54M
40 +1 +3% $7.22M
ORGS icon
68
DELISTED
Orgenesis Inc. Common Stock
ORGS
37 -2 -5% $19.4M
SQZ
69
DELISTED
SQZ Biotechnologies Company
SQZ
36 +36 – $234M
BLCM
70
DELISTED
Bellicum Pharmaceuticals, Inc.
BLCM
34 +12 +55% $5.76M
ONCS
71
DELISTED
OncoSec Medical Incorporated
ONCS
31 +6 +24% $27.4M
GNPX icon
72
Genprex
GNPX
$1.79M
28 +6 +27% $28.8M
INMB icon
73
INmune Bio
INMB
$44.4M
26 -2 -7% $15M
CAPR icon
74
Capricor Therapeutics
CAPR
$392M
25 0 0% $5.14M
IMNN icon
75
Imunon
IMNN
$5.89M
25 -9 -26% $2.28M