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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
ESLA icon
101
Estrella Immunopharma
ESLA
$14M
9 +1 +13% $8.18M
NCEL icon
102
NewcelX Ltd
NCEL
$15.3M
7 +1 +17% $7.11M
TCBP
103
DELISTED
TC BioPharm (Holdings) plc American Depositary Shares
TCBP
6 +3 +100% $380K
KRBP
104
DELISTED
Kiromic BioPharma, Inc. Common Stock
KRBP
5 -2 -29% $6.13K
ATNX
105
DELISTED
Athenex, Inc. Common Stock
ATNX
4 -26 -87% $8.93K
BLCM
106
DELISTED
Bellicum Pharmaceuticals, Inc.
BLCM
4 -21 -84% $173K
GNTA icon
107
Genenta Science
GNTA
$32.5M
4 +2 +100% $2.73M
PTE
108
DELISTED
PolarityTE, Inc. Common Stock
PTE
3 -20 -87% $20
CYAD
109
DELISTED
Celyad Oncology SA American Depositary Shares
CYAD
2 -6 -75% $9.27K
GDTC icon
110
CytoMed Therapeutics
GDTC
$10.1M
1 +1 – $165
SIOX
111
DELISTED
Sio Gene Therapies Inc. Common Stock
SIOX
1 -3 -75% $26K
ONCS
112
DELISTED
OncoSec Medical Incorporated
ONCS
0 -12 -100% $0
RUBY
113
DELISTED
Rubius Therapeutics, Inc
RUBY
0 -7 -100% $0
TCRR
114
DELISTED
TCR2 Therapeutics Inc. Common Stock
TCRR
0 -59 -100% $0
AGTC
115
DELISTED
Applied Genetic Technologies Corporation
AGTC
– – – –
AKUS
116
DELISTED
Akouos Inc
AKUS
– – – –
ARTV icon
117
Artiva Biotherapeutics
ARTV
$294M
– – – –
CRGX icon
118
DELISTED
CARGO Therapeutics
CRGX
– – – –
ENGN icon
119
enGene Therapeutics
ENGN
$110M
– – – –
FBLG icon
120
FibroBiologics
FBLG
$7.29M
– – – –
GUTS icon
121
Fractyl Health
GUTS
$54.3M
– – – –
KYTX icon
122
Kyverna Therapeutics
KYTX
$364M
– – – –
LOGC
123
DELISTED
LogicBio Therapeutics, Inc. Common Stock
LOGC
– – – –
LXEO icon
124
Lexeo Therapeutics
LXEO
$227M
– – – –
MGX icon
125
Metagenomi Therapeutics
MGX
$32.3M
– – – –