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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
IMMX icon
101
Immix Biopharma
IMMX
$720M
12 -6 -33% $730K
INKT icon
102
MiNK Therapeutics
INKT
$50.7M
12 -4 -25% $1.15M
ONCS
103
DELISTED
OncoSec Medical Incorporated
ONCS
12 -5 -29% $665K
ERNA icon
104
Eterna Therapeutics
ERNA
$2.53M
10 -1 -9% $1.14M
CYAD
105
DELISTED
Celyad Oncology SA American Depositary Shares
CYAD
8 0 0% $6.29M
ESLA icon
106
Estrella Immunopharma
ESLA
$23.3M
8 -5 -38% $8.09M
COYA icon
107
Coya Therapeutics
COYA
$102M
7 +3 +75% $4.37M
KRBP
108
DELISTED
Kiromic BioPharma, Inc. Common Stock
KRBP
7 -5 -42% $78.2K
RUBY
109
DELISTED
Rubius Therapeutics, Inc
RUBY
7 -35 -83% $61.3K
NCEL icon
110
NewcelX Ltd
NCEL
$16.5M
6 +2 +50% $9.62M
SIOX
111
DELISTED
Sio Gene Therapies Inc. Common Stock
SIOX
4 -33 -89% $1.13M
TCBP
112
DELISTED
TC BioPharm (Holdings) plc American Depositary Shares
TCBP
3 +2 +200% $207K
GNTA icon
113
Genenta Science
GNTA
$32.3M
2 -2 -50% $274K
SCPS
114
DELISTED
Scopus BioPharma Inc. Common Stock
SCPS
0 -1 -100% $0
AGTC
115
DELISTED
Applied Genetic Technologies Corporation
AGTC
– – – –
AKUS
116
DELISTED
Akouos Inc
AKUS
– – – –
ARTV icon
117
Artiva Biotherapeutics
ARTV
$296M
– – – –
CRGX icon
118
DELISTED
CARGO Therapeutics
CRGX
– – – –
ENGN icon
119
enGene Therapeutics
ENGN
$115M
– – – –
FBLG icon
120
FibroBiologics
FBLG
$7.08M
– – – –
GDTC icon
121
CytoMed Therapeutics
GDTC
$10.4M
– – – –
GUTS icon
122
Fractyl Health
GUTS
$55.2M
– – – –
KYTX icon
123
Kyverna Therapeutics
KYTX
$369M
– – – –
LOGC
124
DELISTED
LogicBio Therapeutics, Inc. Common Stock
LOGC
– – – –
LXEO icon
125
Lexeo Therapeutics
LXEO
$227M
– – – –