← All themes Genomics & Gene Editing

Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
INAB icon
101
IN8bio
INAB
$11.7M
– – – –
INKT icon
102
MiNK Therapeutics
INKT
$50.7M
– – – –
IPSC icon
103
Century Therapeutics
IPSC
$272M
– – – –
KRBP
104
DELISTED
Kiromic BioPharma, Inc. Common Stock
KRBP
– – – –
KYTX icon
105
Kyverna Therapeutics
KYTX
$369M
– – – –
LGVN
106
Longeveron
LGVN
$4.78M
– – – –
LXEO icon
107
Lexeo Therapeutics
LXEO
$227M
– – – –
LYEL icon
108
Lyell Immunopharma
LYEL
$201M
– – – –
MGX icon
109
Metagenomi Therapeutics
MGX
$31.9M
– – – –
NCEL icon
110
NewcelX Ltd
NCEL
$16.5M
– – – –
NKGN icon
111
DELISTED
NKGen Biotech, Inc. Common Stock
NKGN
– – – –
NKTX icon
112
Nkarta
NKTX
$138M
– – – –
OBX
113
Obsidian Therapeutics
OBX
$754M
– – – –
PMCB icon
114
PharmaCyte Biotech
PMCB
$3.84M
– – – –
PRME icon
115
Prime Medicine
PRME
$655M
– – – –
PROK icon
116
ProKidney
PROK
$305M
– – – –
PSTX icon
117
DELISTED
Poseida Therapeutics, Inc. Common Stock
PSTX
– – – –
SANA icon
118
Sana Biotechnology
SANA
$742M
– – – –
SCPS
119
DELISTED
Scopus BioPharma Inc. Common Stock
SCPS
– – – –
SCTX
120
Scribe Therapeutics Inc
SCTX
$392M
– – – –
SGTX
121
DELISTED
Sigilon Therapeutics, Inc. Common Stock
SGTX
– – – –
SLBT
122
SL Science Holding Ltd
SLBT
$869M
– – – –
SNTI icon
123
Senti Biosciences Holdings
SNTI
$8.14M
– – – –
SQZ
124
DELISTED
SQZ Biotechnologies Company
SQZ
– – – –
TCBP
125
DELISTED
TC BioPharm (Holdings) plc American Depositary Shares
TCBP
– – – –