← All themes Genomics & Gene Editing

Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
KRBP
101
DELISTED
Kiromic BioPharma, Inc. Common Stock
KRBP
– – – –
KYTX icon
102
Kyverna Therapeutics
KYTX
$364M
– – – –
LEGN icon
103
Legend Biotech
LEGN
$3.84B
– – – –
LGVN
104
Longeveron
LGVN
$4.56M
– – – –
LXEO icon
105
Lexeo Therapeutics
LXEO
$224M
– – – –
LYEL icon
106
Lyell Immunopharma
LYEL
$199M
– – – –
MGX icon
107
Metagenomi Therapeutics
MGX
$31.9M
– – – –
NCEL icon
108
NewcelX Ltd
NCEL
$15.4M
– – – –
NKGN icon
109
DELISTED
NKGen Biotech, Inc. Common Stock
NKGN
– – – –
NKTX icon
110
Nkarta
NKTX
$138M
– – – –
OBX
111
Obsidian Therapeutics
OBX
$758M
– – – –
PASG icon
112
Passage Bio
PASG
$11.6M
– – – –
PMCB icon
113
PharmaCyte Biotech
PMCB
$3.85M
– – – –
PRME icon
114
Prime Medicine
PRME
$628M
– – – –
PROK icon
115
ProKidney
PROK
$305M
– – – –
PSTX icon
116
DELISTED
Poseida Therapeutics, Inc. Common Stock
PSTX
– – – –
RCOR
117
DELISTED
Renovacor, Inc.
RCOR
– – – –
SANA icon
118
Sana Biotechnology
SANA
$733M
– – – –
SCPS
119
DELISTED
Scopus BioPharma Inc. Common Stock
SCPS
– – – –
SCTX
120
Scribe Therapeutics Inc
SCTX
$392M
– – – –
SGTX
121
DELISTED
Sigilon Therapeutics, Inc. Common Stock
SGTX
– – – –
SLBT
122
SL Science Holding Ltd
SLBT
$948M
– – – –
SNTI icon
123
Senti Biosciences Holdings
SNTI
$7.66M
– – – –
SQZ
124
DELISTED
SQZ Biotechnologies Company
SQZ
– – – –
TCBP
125
DELISTED
TC BioPharm (Holdings) plc American Depositary Shares
TCBP
– – – –