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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
NCEL icon
101
NewcelX Ltd
NCEL
$15.1M
– – – –
NKGN icon
102
DELISTED
NKGen Biotech, Inc. Common Stock
NKGN
– – – –
NKTX icon
103
Nkarta
NKTX
$145M
– – – –
NTLA icon
104
Intellia Therapeutics
NTLA
$1.6B
– – – –
OBX
105
Obsidian Therapeutics
OBX
$755M
– – – –
ORGS icon
106
DELISTED
Orgenesis Inc. Common Stock
ORGS
– – – –
ORTX
107
DELISTED
Orchard Therapeutics plc American Depositary Shares
ORTX
– – – –
PASG icon
108
Passage Bio
PASG
$11.8M
– – – –
PMCB icon
109
PharmaCyte Biotech
PMCB
$3.74M
– – – –
PRME icon
110
Prime Medicine
PRME
$568M
– – – –
PROK icon
111
ProKidney
PROK
$307M
– – – –
PSTX icon
112
DELISTED
Poseida Therapeutics, Inc. Common Stock
PSTX
– – – –
RCOR
113
DELISTED
Renovacor, Inc.
RCOR
– – – –
RNAC icon
114
Cartesian Therapeutics
RNAC
$192M
– – – –
RUBY
115
DELISTED
Rubius Therapeutics, Inc
RUBY
– – – –
SANA icon
116
Sana Biotechnology
SANA
$698M
– – – –
SCPS
117
DELISTED
Scopus BioPharma Inc. Common Stock
SCPS
– – – –
SCTX
118
Scribe Therapeutics Inc
SCTX
$393M
– – – –
SGTX
119
DELISTED
Sigilon Therapeutics, Inc. Common Stock
SGTX
– – – –
SLBT
120
SL Science Holding Ltd
SLBT
$869M
– – – –
SLDB icon
121
Solid Biosciences
SLDB
$585M
– – – –
SNTI icon
122
Senti Biosciences Holdings
SNTI
$7.5M
– – – –
SQZ
123
DELISTED
SQZ Biotechnologies Company
SQZ
– – – –
TCBP
124
DELISTED
TC BioPharm (Holdings) plc American Depositary Shares
TCBP
– – – –
TCRR
125
DELISTED
TCR2 Therapeutics Inc. Common Stock
TCRR
– – – –