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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
101	101 Nkarta NKTX $143M	–	–	–	–
102	102 Intellia Therapeutics NTLA $1.63B	–	–	–	–
103	OBX 103 Obsidian Therapeutics OBX $759M	–	–	–	–
104	104 DELISTED Orgenesis Inc. Common Stock ORGS	–	–	–	–
105	ORTX 105 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	–	–	–	–
106	106 Passage Bio PASG $12.5M	–	–	–	–
107	107 PharmaCyte Biotech PMCB $3.86M	–	–	–	–
108	108 Prime Medicine PRME $635M	–	–	–	–
109	109 ProKidney PROK $303M	–	–	–	–
110	110 DELISTED Poseida Therapeutics, Inc. Common Stock PSTX	–	–	–	–
111	RCOR 111 DELISTED Renovacor, Inc. RCOR	–	–	–	–
112	112 Regenxbio RGNX $459M	–	–	–	–
113	113 Cartesian Therapeutics RNAC $199M	–	–	–	–
114	RUBY 114 DELISTED Rubius Therapeutics, Inc RUBY	–	–	–	–
115	115 Sana Biotechnology SANA $736M	–	–	–	–
116	SCPS 116 DELISTED Scopus BioPharma Inc. Common Stock SCPS	–	–	–	–
117	SCTX 117 Scribe Therapeutics Inc SCTX $388M	–	–	–	–
118	SGTX 118 DELISTED Sigilon Therapeutics, Inc. Common Stock SGTX	–	–	–	–
119	SLBT 119 SL Science Holding Ltd SLBT $925M	–	–	–	–
120	120 Solid Biosciences SLDB $603M	–	–	–	–
121	121 Senti Biosciences Holdings SNTI $7.56M	–	–	–	–
122	SQZ 122 DELISTED SQZ Biotechnologies Company SQZ	–	–	–	–
123	TCBP 123 DELISTED TC BioPharm (Holdings) plc American Depositary Shares TCBP	–	–	–	–
124	TCRR 124 DELISTED TCR2 Therapeutics Inc. Common Stock TCRR	–	–	–	–
125	125 TScan Therapeutics TCRX $15.9M	–	–	–	–