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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
IRD icon
76
Opus Genetics
IRD
$337M
34 -3 -8% $10.8M
SLDB icon
77
Solid Biosciences
SLDB
$615M
34 -24 -41% $85.3M
BLCM
78
DELISTED
Bellicum Pharmaceuticals, Inc.
BLCM
33 +5 +18% $1.23M
GRCL
79
DELISTED
Gracell Biotechnologies Inc. American Depositary Shares
GRCL
33 0 0% $70M
PLUR icon
80
Pluri
PLUR
$11.9M
33 -3 -8% $655K
PTE
81
DELISTED
PolarityTE, Inc. Common Stock
PTE
32 +5 +19% $449K
SGTX
82
DELISTED
Sigilon Therapeutics, Inc. Common Stock
SGTX
32 -1 -3% $6.12M
CAPR icon
83
Capricor Therapeutics
CAPR
$423M
30 -1 -3% $9.94M
PMCB icon
84
PharmaCyte Biotech
PMCB
$3.84M
30 -1 -3% $9.93M
TCRX icon
85
TScan Therapeutics
TCRX
$16.2M
28 +2 +8% $14.8M
PROK icon
86
ProKidney
PROK
$305M
27 +9 +50% $216M
SNTI icon
87
Senti Biosciences Holdings
SNTI
$8.14M
26 +3 +13% $16.6M
BCDA icon
88
BioCardia
BCDA
$14.2M
25 +2 +9% $4.87M
BNTC icon
89
Benitec Biopharma
BNTC
$295M
25 0 0% $2.09M
SCPX icon
90
DELISTED
Scorpius Holdings, Inc.
SCPX
24 +1 +4% $2M
ACHL
91
DELISTED
Achilles Therapeutics
ACHL
23 -5 -18% $19.5M
CLDI icon
92
Calidi Biotherapeutics
CLDI
$2.25M
23 +3 +15% $39.6M
CADL icon
93
Candel Therapeutics
CADL
$682M
21 -4 -16% $9.7M
ENLV icon
94
Enlivex Ltd
ENLV
$4.46M
21 +3 +17% $1.32M
IMNN icon
95
Imunon
IMNN
$5.95M
21 0 0% $573K
ORGS icon
96
DELISTED
Orgenesis Inc. Common Stock
ORGS
19 -3 -14% $3.02M
CELZ icon
97
Creative Medical Technology
CELZ
$6.21M
18 +1 +6% $157K
GNPX icon
98
Genprex
GNPX
$1.88M
18 -2 -10% $5.85M
IMMX icon
99
Immix Biopharma
IMMX
$720M
18 +6 +50% $1.01M
FRLN
100
DELISTED
Freeline Therapeutics Holdings plc American Depositary Shares
FRLN
17 +3 +21% $18.2M