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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
76	KRBP 76 DELISTED Kiromic BioPharma, Inc. Common Stock KRBP	–	–	–	–
77	77 Krystal Biotech KRYS $9.79B	–	–	–	–
78	78 Kyverna Therapeutics KYTX $351M	–	–	–	–
79	79 Legend Biotech LEGN $3.7B	–	–	–	–
80	LGVN 80 Longeveron LGVN $5.52M	–	–	–	–
81	81 Lakefront Biotherapeutics American Depositary Shares LKFT $1.93B	–	–	–	–
82	82 Lunai Bioworks LNAI $4.05M	–	–	–	–
83	LOGC 83 DELISTED LogicBio Therapeutics, Inc. Common Stock LOGC	–	–	–	–
84	84 Lexeo Therapeutics LXEO $216M	–	–	–	–
85	85 Lyell Immunopharma LYEL $196M	–	–	–	–
86	86 Mustang Bio MBIO $2.8M	–	–	–	–
87	87 Mesoblast MESO $1.79B	–	–	–	–
88	88 MeiraGTx Holdings MGTX $904M	–	–	–	–
89	89 Metagenomi Therapeutics MGX $32.5M	–	–	–	–
90	90 Marker Therapeutics MRKR $14.8M	–	–	–	–
91	91 NewcelX Ltd NCEL $15.1M	–	–	–	–
92	92 Neurogene NGNE $444M	–	–	–	–
93	93 DELISTED NKGen Biotech, Inc. Common Stock NKGN	–	–	–	–
94	94 Nkarta NKTX $145M	–	–	–	–
95	95 Intellia Therapeutics NTLA $1.6B	–	–	–	–
96	OBX 96 Obsidian Therapeutics OBX $755M	–	–	–	–
97	97 Ocugen OCGN $285M	–	–	–	–
98	ONCS 98 DELISTED OncoSec Medical Incorporated ONCS	–	–	–	–
99	99 DELISTED Orgenesis Inc. Common Stock ORGS	–	–	–	–
100	ORTX 100 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	–	–	–	–