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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
51	51 Autolus Therapeutics AUTL $458M	66	-1	-1%	$106M
52	52 DELISTED CERo Therapeutics CERO	65	+13	+25%	$153M
53	AKUS 53 DELISTED Akouos Inc AKUS	64	-2	-3%	$241M
54	54 Fortress Biotech FBIO $63.7M	64	-2	-3%	$25.8M
55	GMDA 55 DELISTED Gamida Cell Ltd. Ordinary Shares GMDA	62	+5	+9%	$38.3M
56	RUBY 56 DELISTED Rubius Therapeutics, Inc RUBY	62	-10	-14%	$29.7M
57	57 Solid Biosciences SLDB $615M	58	-9	-13%	$33.4M
58	58 Cabaletta Bio CABA $263M	54	-1	-2%	$7.76M
59	59 Immatics IMTX $1.09B	54	+5	+10%	$221M
60	60 Century Therapeutics IPSC $272M	54	-2	-4%	$209M
61	61 Taysha Gene Therapies TSHA $1.22B	54	-5	-8%	$27M
62	62 DELISTED NKGen Biotech, Inc. Common Stock NKGN	53	+6	+13%	$143M
63	63 Neurogene NGNE $479M	52	-11	-17%	$12M
64	64 Cellectis CLLS $111M	49	+5	+11%	$23.6M
65	SQZ 65 DELISTED SQZ Biotechnologies Company SQZ	48	-5	-9%	$33.5M
66	ORTX 66 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	47	-3	-6%	$24.7M
67	AGTC 67 DELISTED Applied Genetic Technologies Corporation AGTC	45	-2	-4%	$3.34M
68	68 Marker Therapeutics MRKR $15.3M	45	-3	-6%	$7.56M
69	ATHX 69 DELISTED Athersys, Inc. Common Stock ATHX	44	-71	-62%	$4.11M
70	70 DELISTED BRAINSTORM CELL THERAPUTC BCLI	42	-6	-13%	$17.1M
71	71 Lunai Bioworks LNAI $3.74M	42	-9	-18%	$6.87M
72	DBTX 72 DELISTED Decibel Therapeutics, Inc. Common Stock DBTX	40	-2	-5%	$62.1M
73	SIOX 73 DELISTED Sio Gene Therapies Inc. Common Stock SIOX	40	-1	-2%	$7.62M
74	LOGC 74 DELISTED LogicBio Therapeutics, Inc. Common Stock LOGC	39	-8	-17%	$2.82M
75	75 Opus Genetics IRD $337M	37	-1	-3%	$5.69M