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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
PROK icon
51
ProKidney
PROK
$307M
67 -14 -17% $191M
SLDB icon
52
Solid Biosciences
SLDB
$586M
67 -10 -13% $39.5M
AKUS
53
DELISTED
Akouos Inc
AKUS
66 -8 -11% $165M
CELU icon
54
Celularity
CELU
$42.5M
66 +28 +74% $105M
FBIO icon
55
Fortress Biotech
FBIO
$63.4M
66 -13 -16% $25.9M
NGNE icon
56
Neurogene
NGNE
$444M
63 -18 -22% $21.4M
TSHA icon
57
Taysha Gene Therapies
TSHA
$1.14B
59 -12 -17% $54.7M
GMDA
58
DELISTED
Gamida Cell Ltd. Ordinary Shares
GMDA
57 -2 -3% $25.9M
IPSC icon
59
Century Therapeutics
IPSC
$250M
56 +4 +8% $183M
PSTX icon
60
DELISTED
Poseida Therapeutics, Inc. Common Stock
PSTX
56 -8 -13% $58.1M
CABA icon
61
Cabaletta Bio
CABA
$275M
55 -7 -11% $17.8M
SQZ
62
DELISTED
SQZ Biotechnologies Company
SQZ
53 0 0% $47.1M
CERO icon
63
DELISTED
CERo Therapeutics
CERO
52 +6 +13% $145M
LNAI icon
64
Lunai Bioworks
LNAI
$4.05M
51 +8 +19% $7.64M
ORTX
65
DELISTED
Orchard Therapeutics plc American Depositary Shares
ORTX
50 -12 -19% $30.2M
TNYA icon
66
Tenaya Therapeutics
TNYA
$87.6M
50 0 0% $209M
IMTX icon
67
Immatics
IMTX
$1.07B
49 +2 +4% $187M
BCLI icon
68
DELISTED
BRAINSTORM CELL THERAPUTC
BCLI
48 +9 +23% $11M
MRKR icon
69
Marker Therapeutics
MRKR
$14.8M
48 -1 -2% $7.36M
AGTC
70
DELISTED
Applied Genetic Technologies Corporation
AGTC
47 -6 -11% $8.53M
LOGC
71
DELISTED
LogicBio Therapeutics, Inc. Common Stock
LOGC
47 +1 +2% $3.88M
NKGN icon
72
DELISTED
NKGen Biotech, Inc. Common Stock
NKGN
47 +3 +7% $124M
CLLS icon
73
Cellectis
CLLS
$113M
44 -6 -12% $30.6M
ABEO icon
74
Abeona Therapeutics
ABEO
$249M
42 -12 -22% $4.68M
DBTX
75
DELISTED
Decibel Therapeutics, Inc. Common Stock
DBTX
42 +3 +8% $75.2M