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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
SLDB icon
51
Solid Biosciences
SLDB
$615M
77 -5 -6% $83.2M
AKUS
52
DELISTED
Akouos Inc
AKUS
74 -2 -3% $165M
TSHA icon
53
Taysha Gene Therapies
TSHA
$1.22B
71 +6 +9% $111M
VYGR icon
54
Voyager Therapeutics
VYGR
$127M
70 +11 +19% $171M
AUTL icon
55
Autolus Therapeutics
AUTL
$458M
67 -6 -8% $229M
PSTX icon
56
DELISTED
Poseida Therapeutics, Inc. Common Stock
PSTX
64 -2 -3% $108M
CABA icon
57
Cabaletta Bio
CABA
$263M
62 -4 -6% $36.9M
ORTX
58
DELISTED
Orchard Therapeutics plc American Depositary Shares
ORTX
62 -10 -14% $39.8M
GMDA
59
DELISTED
Gamida Cell Ltd. Ordinary Shares
GMDA
59 -4 -6% $84M
ABEO icon
60
Abeona Therapeutics
ABEO
$266M
54 +2 +4% $10.5M
AGTC
61
DELISTED
Applied Genetic Technologies Corporation
AGTC
53 -2 -4% $16.2M
SQZ
62
DELISTED
SQZ Biotechnologies Company
SQZ
53 +3 +6% $76.6M
IPSC icon
63
Century Therapeutics
IPSC
$272M
52 +2 +4% $279M
CLLS icon
64
Cellectis
CLLS
$111M
50 -6 -11% $55.8M
TNYA icon
65
Tenaya Therapeutics
TNYA
$91.6M
50 +3 +6% $440M
ACLX icon
66
DELISTED
Arcellx
ACLX
49 +49 – $358M
ERNA icon
67
Eterna Therapeutics
ERNA
$2.53M
49 +2 +4% $38.4M
MRKR icon
68
Marker Therapeutics
MRKR
$15.3M
49 -15 -23% $10.3M
SGTX
69
DELISTED
Sigilon Therapeutics, Inc. Common Stock
SGTX
48 -2 -4% $26.8M
IMTX icon
70
Immatics
IMTX
$1.09B
47 -2 -4% $173M
CERO icon
71
DELISTED
CERo Therapeutics
CERO
46 +10 +28% $139M
LOGC
72
DELISTED
LogicBio Therapeutics, Inc. Common Stock
LOGC
46 -11 -19% $8.66M
SNTI icon
73
Senti Biosciences Holdings
SNTI
$8.14M
46 +4 +10% $181M
NKGN icon
74
DELISTED
NKGen Biotech, Inc. Common Stock
NKGN
44 +3 +7% $120M
PTE
75
DELISTED
PolarityTE, Inc. Common Stock
PTE
44 +5 +13% $4.07M