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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
VYGR icon
51
Voyager Therapeutics
VYGR
$127M
69 -9 -12% $58.6M
PSTX icon
52
DELISTED
Poseida Therapeutics, Inc. Common Stock
PSTX
65 -6 -8% $191M
AGTC
53
DELISTED
Applied Genetic Technologies Corporation
AGTC
64 -7 -10% $38.9M
TIL icon
54
Instil Bio
TIL
$41.6M
64 +2 +3% $1.28B
FDMT icon
55
4D Molecular Therapeutics
FDMT
$711M
63 +7 +13% $515M
MRKR icon
56
Marker Therapeutics
MRKR
$15.3M
63 -11 -15% $44.7M
LYEL icon
57
Lyell Immunopharma
LYEL
$201M
62 +10 +19% $1.22B
CABA icon
58
Cabaletta Bio
CABA
$263M
61 -2 -3% $211M
AUTL icon
59
Autolus Therapeutics
AUTL
$458M
59 -10 -14% $164M
ABEO icon
60
Abeona Therapeutics
ABEO
$266M
58 -12 -17% $28.3M
ACET icon
61
Adicet Bio
ACET
$48.1M
58 -7 -11% $156M
LOGC
62
DELISTED
LogicBio Therapeutics, Inc. Common Stock
LOGC
57 -6 -10% $73.2M
SIOX
63
DELISTED
Sio Gene Therapies Inc. Common Stock
SIOX
56 +2 +4% $39.9M
PLUR icon
64
Pluri
PLUR
$11.9M
55 -4 -7% $11.8M
BCLI icon
65
DELISTED
BRAINSTORM CELL THERAPUTC
BCLI
52 -5 -9% $16.9M
IMTX icon
66
Immatics
IMTX
$1.09B
51 +1 +2% $292M
IPSC icon
67
Century Therapeutics
IPSC
$272M
49 +13 +36% $496M
TSHA icon
68
Taysha Gene Therapies
TSHA
$1.22B
48 -1 -2% $362M
PTE
69
DELISTED
PolarityTE, Inc. Common Stock
PTE
47 -1 -2% $6.92M
TNYA icon
70
Tenaya Therapeutics
TNYA
$91.6M
47 +47 – $693M
SGTX
71
DELISTED
Sigilon Therapeutics, Inc. Common Stock
SGTX
45 -7 -13% $109M
ERNA icon
72
Eterna Therapeutics
ERNA
$2.53M
44 +12 +38% $47.3M
SQZ
73
DELISTED
SQZ Biotechnologies Company
SQZ
44 -5 -10% $199M
INMB icon
74
INmune Bio
INMB
$45.8M
41 0 0% $37.7M
MESO icon
75
Mesoblast
MESO
$1.81B
41 -9 -18% $21.2M