← All themes Genomics & Gene Editing

Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
AGTC
51
DELISTED
Applied Genetic Technologies Corporation
AGTC
71 -11 -13% $53.9M
PSTX icon
52
DELISTED
Poseida Therapeutics, Inc. Common Stock
PSTX
71 +9 +15% $279M
ABEO icon
53
Abeona Therapeutics
ABEO
$273M
70 -5 -7% $43.4M
GMDA
54
DELISTED
Gamida Cell Ltd. Ordinary Shares
GMDA
70 -3 -4% $157M
AUTL icon
55
Autolus Therapeutics
AUTL
$458M
69 +6 +10% $170M
ACET icon
56
Adicet Bio
ACET
$47.7M
65 +12 +23% $218M
CABA icon
57
Cabaletta Bio
CABA
$259M
63 -5 -7% $135M
LOGC
58
DELISTED
LogicBio Therapeutics, Inc. Common Stock
LOGC
63 +2 +3% $69.9M
TIL icon
59
Instil Bio
TIL
$42.8M
62 +6 +11% $1.35B
PLUR icon
60
Pluri
PLUR
$12M
59 -1 -2% $17.9M
BCLI icon
61
DELISTED
BRAINSTORM CELL THERAPUTC
BCLI
57 -18 -24% $21.4M
FDMT icon
62
4D Molecular Therapeutics
FDMT
$693M
56 -8 -13% $400M
SIOX
63
DELISTED
Sio Gene Therapies Inc. Common Stock
SIOX
54 -2 -4% $57.7M
LYEL icon
64
Lyell Immunopharma
LYEL
$195M
52 +52 – $1.29B
SGTX
65
DELISTED
Sigilon Therapeutics, Inc. Common Stock
SGTX
52 0 0% $209M
IMTX icon
66
Immatics
IMTX
$1.09B
50 +6 +14% $243M
MESO icon
67
Mesoblast
MESO
$1.81B
50 -2 -4% $28.9M
SQZ
68
DELISTED
SQZ Biotechnologies Company
SQZ
49 +2 +4% $196M
TSHA icon
69
Taysha Gene Therapies
TSHA
$1.22B
49 +3 +7% $389M
PTE
70
DELISTED
PolarityTE, Inc. Common Stock
PTE
48 -2 -4% $11.1M
DBTX
71
DELISTED
Decibel Therapeutics, Inc. Common Stock
DBTX
46 -8 -15% $168M
SNTI icon
72
Senti Biosciences Holdings
SNTI
$7.62M
44 +44 – $207M
INMB icon
73
INmune Bio
INMB
$44.4M
41 +8 +24% $30.6M
IMNN icon
74
Imunon
IMNN
$6M
37 -3 -8% $11.5M
LNAI icon
75
Lunai Bioworks
LNAI
$4.01M
37 -4 -10% $13.3M