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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
PTE
51
DELISTED
PolarityTE, Inc. Common Stock
PTE
52 -13 -20% $8.3M
AUTL icon
52
Autolus Therapeutics
AUTL
$458M
50 -1 -2% $230M
GBIO icon
53
DELISTED
Generation Bio
GBIO
48 +48 – $581M
LOGC
54
DELISTED
LogicBio Therapeutics, Inc. Common Stock
LOGC
43 0 0% $97.7M
MESO icon
55
Mesoblast
MESO
$1.81B
43 +9 +26% $32.1M
CELU icon
56
Celularity
CELU
$43.2M
42 +7 +20% $209M
CARM icon
57
DELISTED
Carisma Therapeutics
CARM
40 +4 +11% $13.5M
ORGS icon
58
DELISTED
Orgenesis Inc. Common Stock
ORGS
40 +24 +150% $27.5M
SIOX
59
DELISTED
Sio Gene Therapies Inc. Common Stock
SIOX
40 -2 -5% $33.7M
IMNN icon
60
Imunon
IMNN
$5.95M
37 +18 +95% $15.2M
CAPR icon
61
Capricor Therapeutics
CAPR
$423M
33 +15 +83% $4.32M
LNAI icon
62
Lunai Bioworks
LNAI
$3.74M
33 +1 +3% $10.4M
IMTX icon
63
Immatics
IMTX
$1.09B
32 +5 +19% $143M
GNPX icon
64
Genprex
GNPX
$1.88M
29 +20 +222% $15.9M
BLCM
65
DELISTED
Bellicum Pharmaceuticals, Inc.
BLCM
27 -2 -7% $7.68M
GMDA
66
DELISTED
Gamida Cell Ltd. Ordinary Shares
GMDA
27 +14 +108% $73.3M
OCGN icon
67
Ocugen
OCGN
$276M
21 +5 +31% $577K
INMB icon
68
INmune Bio
INMB
$45.8M
16 +3 +23% $1.88M
ONCS
69
DELISTED
OncoSec Medical Incorporated
ONCS
16 -4 -20% $1.89M
SCPX icon
70
DELISTED
Scorpius Holdings, Inc.
SCPX
15 +6 +67% $8.84M
IRD icon
71
Opus Genetics
IRD
$337M
14 -3 -18% $898K
BCDA icon
72
BioCardia
BCDA
$14.2M
12 +5 +71% $2.85M
CYAD
73
DELISTED
Celyad Oncology SA American Depositary Shares
CYAD
9 +1 +13% $9.23M
ENLV icon
74
Enlivex Ltd
ENLV
$4.46M
7 +1 +17% $1.8M
ERNA icon
75
Eterna Therapeutics
ERNA
$2.53M
6 -1 -14% $499K