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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

Name Funds
holding
Growth Growth % Fund
value
CRBU icon
26
Caribou Biosciences
CRBU
$48.2M
120 +16 +15% $203M
DTIL icon
27
Precision BioSciences
DTIL
$167M
119 -33 -22% $93.5M
SANA icon
28
Sana Biotechnology
SANA
$730M
116 -1 -0.9% $808M
ATHX
29
DELISTED
Athersys, Inc. Common Stock
ATHX
115 -10 -8% $10.9M
NKTX icon
30
Nkarta
NKTX
$143M
115 +31 +37% $537M
MGTX icon
31
MeiraGTx Holdings
MGTX
$933M
108 +5 +5% $216M
ACET icon
32
Adicet Bio
ACET
$47.3M
101 +14 +16% $556M
LCTX icon
33
Lineage Cell Therapeutics
LCTX
$241M
101 -9 -8% $103M
TIL icon
34
Instil Bio
TIL
$42.8M
98 +20 +26% $551M
RNAC icon
35
Cartesian Therapeutics
RNAC
$199M
92 -10 -10% $79.7M
GBIO icon
36
DELISTED
Generation Bio
GBIO
91 +3 +3% $364M
FDMT icon
37
4D Molecular Therapeutics
FDMT
$686M
89 +9 +11% $182M
PASG icon
38
Passage Bio
PASG
$12.5M
85 -23 -21% $99.6M
TCRR
39
DELISTED
TCR2 Therapeutics Inc. Common Stock
TCRR
83 -11 -12% $72.2M
LKFT icon
40
Lakefront Biotherapeutics American Depositary Shares
LKFT
$1.97B
81 -8 -9% $720M
VYGR icon
41
Voyager Therapeutics
VYGR
$127M
78 +8 +11% $142M
ADAP
42
DELISTED
Adaptimmune Therapeutics
ADAP
77 -3 -4% $195M
ADVM icon
43
DELISTED
Adverum Biotechnologies
ADVM
77 -15 -16% $70M
ATNX
44
DELISTED
Athenex, Inc. Common Stock
ATNX
76 -15 -16% $14.7M
LYEL icon
45
Lyell Immunopharma
LYEL
$193M
75 -4 -5% $689M
CARM icon
46
DELISTED
Carisma Therapeutics
CARM
73 -11 -13% $23.1M
RUBY
47
DELISTED
Rubius Therapeutics, Inc
RUBY
72 -45 -38% $66.6M
MBIO icon
48
Mustang Bio
MBIO
$2.91M
71 -10 -12% $10.3M
ACLX icon
49
DELISTED
Arcellx
ACLX
68 +19 +39% $622M
AUTL icon
50
Autolus Therapeutics
AUTL
$458M
67 0 0% $144M