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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	ATNX 26 DELISTED Athenex, Inc. Common Stock ATNX	122	-10	-8%	$233M
27	ISEE 27 DELISTED IVERIC bio, Inc. Common Stock ISEE	115	-5	-4%	$496M
28	28 Krystal Biotech KRYS $9.85B	113	+5	+5%	$1.27B
29	RUBY 29 DELISTED Rubius Therapeutics, Inc RUBY	105	+18	+21%	$2.23B
30	30 Solid Biosciences SLDB $604M	104	+29	+39%	$438M
31	31 Lineage Cell Therapeutics LCTX $243M	102	+13	+15%	$142M
32	32 Voyager Therapeutics VYGR $126M	101	0	0%	$130M
33	33 Cartesian Therapeutics RNAC $199M	98	+3	+3%	$878M
34	34 Nkarta NKTX $142M	97	+8	+9%	$867M
35	35 Mustang Bio MBIO $2.88M	95	+2	+2%	$80.6M
36	36 Passage Bio PASG $12.5M	89	+18	+25%	$786M
37	37 DELISTED Generation Bio GBIO	88	+20	+29%	$1.27B
38	38 Fortress Biotech FBIO $64.7M	85	-2	-2%	$110M
39	ADAP 39 DELISTED Adaptimmune Therapeutics ADAP	84	-3	-3%	$624M
40	ORTX 40 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	83	+6	+8%	$546M
41	AGTC 41 DELISTED Applied Genetic Technologies Corporation AGTC	82	+16	+24%	$93.3M
42	42 Neurogene NGNE $478M	82	-2	-2%	$342M
43	43 Ocugen OCGN $275M	82	+39	+91%	$167M
44	44 MeiraGTx Holdings MGTX $944M	81	-10	-11%	$385M
45	45 Cellectis CLLS $111M	80	-10	-11%	$308M
46	46 Sana Biotechnology SANA $730M	78	+78	–	$3.1B
47	AKUS 47 DELISTED Akouos Inc AKUS	77	+17	+28%	$461M
48	48 DELISTED Carisma Therapeutics CARM	76	+20	+36%	$104M
49	49 Abeona Therapeutics ABEO $270M	75	+2	+3%	$58.4M
50	50 DELISTED BRAINSTORM CELL THERAPUTC BCLI	75	-15	-17%	$32.1M