← All themes Genomics & Gene Editing

Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	TCRR 26 DELISTED TCR2 Therapeutics Inc. Common Stock TCRR	118	+36	+44%	$1.07B
27	27 Lakefront Biotherapeutics American Depositary Shares LKFT $1.96B	116	-3	-3%	$452M
28	28 Krystal Biotech KRYS $9.77B	108	+10	+10%	$835M
29	29 Voyager Therapeutics VYGR $127M	101	-9	-8%	$198M
30	30 Cartesian Therapeutics RNAC $199M	95	+16	+20%	$154M
31	31 Mustang Bio MBIO $2.8M	93	+18	+24%	$75.4M
32	32 MeiraGTx Holdings MGTX $950M	91	+6	+7%	$405M
33	33 DELISTED BRAINSTORM CELL THERAPUTC BCLI	90	+10	+13%	$38.7M
34	34 Cellectis CLLS $111M	90	+16	+22%	$442M
35	35 Lineage Cell Therapeutics LCTX $232M	89	+14	+19%	$96.9M
36	36 Nkarta NKTX $138M	89	+33	+59%	$1.56B
37	ADAP 37 DELISTED Adaptimmune Therapeutics ADAP	87	+8	+10%	$637M
38	38 Fortress Biotech FBIO $63.7M	87	+10	+13%	$101M
39	RUBY 39 DELISTED Rubius Therapeutics, Inc RUBY	87	+3	+4%	$572M
40	40 Neurogene NGNE $479M	84	+3	+4%	$391M
41	ORTX 41 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	77	+5	+7%	$247M
42	42 Solid Biosciences SLDB $615M	75	+13	+21%	$414M
43	43 Abeona Therapeutics ABEO $266M	73	-5	-6%	$50.9M
44	44 Passage Bio PASG $11.6M	71	+1	+1%	$818M
45	45 DELISTED Generation Bio GBIO	68	+15	+28%	$906M
46	AGTC 46 DELISTED Applied Genetic Technologies Corporation AGTC	66	-5	-7%	$57.3M
47	47 Celularity CELU $43.2M	64	+9	+16%	$166M
48	SIOX 48 DELISTED Sio Gene Therapies Inc. Common Stock SIOX	62	+12	+24%	$39.7M
49	49 Legend Biotech LEGN $3.85B	61	+11	+22%	$717M
50	AKUS 50 DELISTED Akouos Inc AKUS	60	+3	+5%	$637M