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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	26 DELISTED BioLife Solutions BLFS	108	+26	+32%	$641M
27	ISEE 27 DELISTED IVERIC bio, Inc. Common Stock ISEE	100	-19	-16%	$431M
28	28 Krystal Biotech KRYS $9.77B	98	-12	-11%	$623M
29	29 MeiraGTx Holdings MGTX $950M	85	+4	+5%	$293M
30	RUBY 30 DELISTED Rubius Therapeutics, Inc RUBY	84	-2	-2%	$382M
31	TCRR 31 DELISTED TCR2 Therapeutics Inc. Common Stock TCRR	82	+18	+28%	$557M
32	32 Neurogene NGNE $479M	81	+7	+9%	$331M
33	33 DELISTED BRAINSTORM CELL THERAPUTC BCLI	80	+4	+5%	$115M
34	ADAP 34 DELISTED Adaptimmune Therapeutics ADAP	79	+2	+3%	$1.04B
35	35 Cartesian Therapeutics RNAC $199M	79	-2	-2%	$148M
36	36 Abeona Therapeutics ABEO $266M	78	-5	-6%	$36.7M
37	37 Fortress Biotech FBIO $63.7M	77	+4	+5%	$119M
38	38 Lineage Cell Therapeutics LCTX $250M	75	-19	-20%	$50.2M
39	39 Mustang Bio MBIO $2.93M	75	+2	+3%	$53M
40	40 Cellectis CLLS $111M	74	-5	-6%	$263M
41	ORTX 41 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	72	-9	-11%	$266M
42	AGTC 42 DELISTED Applied Genetic Technologies Corporation AGTC	71	+6	+9%	$74.5M
43	43 Passage Bio PASG $11.6M	70	+4	+6%	$403M
44	44 Solid Biosciences SLDB $615M	62	-4	-6%	$53.2M
45	45 Marker Therapeutics MRKR $15.3M	58	-5	-8%	$21.2M
46	AKUS 46 DELISTED Akouos Inc AKUS	57	+1	+2%	$696M
47	47 Nkarta NKTX $138M	56	+56	–	$760M
48	48 Celularity CELU $43.2M	55	+13	+31%	$193M
49	49 Cabaletta Bio CABA $263M	54	+2	+4%	$177M
50	50 DELISTED Generation Bio GBIO	53	+5	+10%	$896M