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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	26 Krystal Biotech KRYS $9.79B	110	+20	+22%	$589M
27	ATNX 27 DELISTED Athenex, Inc. Common Stock ATNX	104	+3	+3%	$624M
28	28 Lineage Cell Therapeutics LCTX $232M	94	-3	-3%	$48.5M
29	RUBY 29 DELISTED Rubius Therapeutics, Inc RUBY	86	+10	+13%	$462M
30	30 Abeona Therapeutics ABEO $249M	83	+3	+4%	$126M
31	31 DELISTED BioLife Solutions BLFS	82	+7	+9%	$244M
32	32 MeiraGTx Holdings MGTX $904M	81	-2	-2%	$262M
33	ORTX 33 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	81	+7	+9%	$392M
34	34 Cartesian Therapeutics RNAC $192M	81	+20	+33%	$174M
35	35 Cellectis CLLS $113M	79	+14	+22%	$247M
36	ADAP 36 DELISTED Adaptimmune Therapeutics ADAP	77	+30	+64%	$1.28B
37	37 Legend Biotech LEGN $3.7B	77	+77	–	$1.04B
38	38 DELISTED BRAINSTORM CELL THERAPUTC BCLI	76	+25	+49%	$70M
39	39 Neurogene NGNE $444M	74	+14	+23%	$417M
40	40 Fortress Biotech FBIO $63.4M	73	+18	+33%	$60.6M
41	41 Mustang Bio MBIO $2.8M	73	+9	+14%	$45.9M
42	42 Passage Bio PASG $11.8M	66	+21	+47%	$863M
43	43 Solid Biosciences SLDB $586M	66	-5	-7%	$79.1M
44	AGTC 44 DELISTED Applied Genetic Technologies Corporation AGTC	65	+6	+10%	$90.6M
45	TCRR 45 DELISTED TCR2 Therapeutics Inc. Common Stock TCRR	64	+14	+28%	$234M
46	46 Marker Therapeutics MRKR $14.8M	63	-2	-3%	$29.4M
47	AKUS 47 DELISTED Akouos Inc AKUS	56	+56	–	$625M
48	48 Adicet Bio ACET $45.8M	53	+2	+4%	$36.2M
49	49 Pluri PLUR $11.7M	53	+24	+83%	$20M
50	50 Cabaletta Bio CABA $275M	52	+11	+27%	$183M