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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	26 BridgeBio Pharma BBIO $13.1B	95	+7	+8%	$3.27B
27	27 Krystal Biotech KRYS $9.77B	90	0	0%	$502M
28	28 MeiraGTx Holdings MGTX $950M	83	-2	-2%	$270M
29	29 Abeona Therapeutics ABEO $266M	80	-7	-8%	$93.4M
30	RUBY 30 DELISTED Rubius Therapeutics, Inc RUBY	76	0	0%	$335M
31	31 DELISTED BioLife Solutions BLFS	75	-5	-6%	$116M
32	ISEE 32 DELISTED IVERIC bio, Inc. Common Stock ISEE	75	+7	+10%	$113M
33	ORTX 33 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	74	-7	-9%	$484M
34	34 Solid Biosciences SLDB $615M	71	+2	+3%	$46.9M
35	35 Cellectis CLLS $111M	65	+5	+8%	$133M
36	36 Marker Therapeutics MRKR $15.3M	65	0	0%	$28.3M
37	PTE 37 DELISTED PolarityTE, Inc. Common Stock PTE	65	-1	-2%	$11.1M
38	38 Mustang Bio MBIO $2.93M	64	+9	+16%	$24M
39	39 Cartesian Therapeutics RNAC $199M	61	+23	+61%	$136M
40	40 Neurogene NGNE $479M	60	+5	+9%	$259M
41	AGTC 41 DELISTED Applied Genetic Technologies Corporation AGTC	59	+7	+13%	$49.3M
42	42 Fortress Biotech FBIO $63.7M	55	+1	+2%	$17.4M
43	43 Adicet Bio ACET $48.1M	51	-3	-6%	$13.6M
44	44 Autolus Therapeutics AUTL $458M	51	-4	-7%	$96.4M
45	45 DELISTED BRAINSTORM CELL THERAPUTC BCLI	51	+8	+19%	$17.2M
46	TCRR 46 DELISTED TCR2 Therapeutics Inc. Common Stock TCRR	50	+5	+11%	$110M
47	ADAP 47 DELISTED Adaptimmune Therapeutics ADAP	47	+4	+9%	$255M
48	48 Passage Bio PASG $11.6M	45	+45	–	$458M
49	LOGC 49 DELISTED LogicBio Therapeutics, Inc. Common Stock LOGC	43	-1	-2%	$55.2M
50	SIOX 50 DELISTED Sio Gene Therapies Inc. Common Stock SIOX	42	-6	-13%	$28.4M