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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	26 Krystal Biotech KRYS $9.79B	90	+5	+6%	$635M
27	27 BridgeBio Pharma BBIO $12.7B	88	+13	+17%	$3.67B
28	28 Abeona Therapeutics ABEO $249M	87	+8	+10%	$180M
29	29 MeiraGTx Holdings MGTX $904M	85	+4	+5%	$334M
30	ORTX 30 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	81	+19	+31%	$895M
31	31 DELISTED BioLife Solutions BLFS	80	0	0%	$168M
32	RUBY 32 DELISTED Rubius Therapeutics, Inc RUBY	76	+1	+1%	$771M
33	33 Solid Biosciences SLDB $585M	69	0	0%	$88.5M
34	ISEE 34 DELISTED IVERIC bio, Inc. Common Stock ISEE	68	+20	+42%	$270M
35	PTE 35 DELISTED PolarityTE, Inc. Common Stock PTE	66	+2	+3%	$20.2M
36	36 Marker Therapeutics MRKR $14.8M	65	-8	-11%	$44.5M
37	37 Cellectis CLLS $113M	60	-4	-6%	$226M
38	38 Autolus Therapeutics AUTL $450M	55	+12	+28%	$177M
39	39 Mustang Bio MBIO $2.8M	55	0	0%	$35.8M
40	40 Neurogene NGNE $444M	55	+19	+53%	$241M
41	41 Adicet Bio ACET $45.8M	54	-2	-4%	$26.8M
42	42 Fortress Biotech FBIO $63.4M	54	+5	+10%	$18.4M
43	AGTC 43 DELISTED Applied Genetic Technologies Corporation AGTC	52	-3	-5%	$37.9M
44	BLCM 44 DELISTED Bellicum Pharmaceuticals, Inc. BLCM	51	-16	-24%	$22.6M
45	SIOX 45 DELISTED Sio Gene Therapies Inc. Common Stock SIOX	48	0	0%	$14.8M
46	46 DELISTED Carisma Therapeutics CARM	46	+9	+24%	$18.8M
47	TCRR 47 DELISTED TCR2 Therapeutics Inc. Common Stock TCRR	45	+5	+13%	$203M
48	LOGC 48 DELISTED LogicBio Therapeutics, Inc. Common Stock LOGC	44	+4	+10%	$86M
49	ADAP 49 DELISTED Adaptimmune Therapeutics ADAP	43	-6	-12%	$77.9M
50	50 DELISTED BRAINSTORM CELL THERAPUTC BCLI	43	+4	+10%	$8.85M