← All themes Genomics & Gene Editing

Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	26 MeiraGTx Holdings MGTX $940M	81	+13	+19%	$253M
27	27 DELISTED BioLife Solutions BLFS	80	+7	+10%	$170M
28	28 Abeona Therapeutics ABEO $269M	79	-19	-19%	$64.6M
29	29 BridgeBio Pharma BBIO $13.1B	75	+14	+23%	$2.22B
30	RUBY 30 DELISTED Rubius Therapeutics, Inc RUBY	75	+6	+9%	$632M
31	31 Marker Therapeutics MRKR $15M	73	+3	+4%	$87.6M
32	32 Precision BioSciences DTIL $168M	72	+9	+14%	$179M
33	33 Solid Biosciences SLDB $603M	69	-5	-7%	$332M
34	BLCM 34 DELISTED Bellicum Pharmaceuticals, Inc. BLCM	67	-12	-15%	$20.7M
35	35 Cellectis CLLS $111M	64	-6	-9%	$137M
36	PTE 36 DELISTED PolarityTE, Inc. Common Stock PTE	64	-10	-14%	$28.7M
37	ORTX 37 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	62	-6	-9%	$755M
38	38 Adicet Bio ACET $47.6M	56	+8	+17%	$169M
39	AGTC 39 DELISTED Applied Genetic Technologies Corporation AGTC	55	+9	+20%	$34.1M
40	40 Mustang Bio MBIO $2.88M	55	0	0%	$35.3M
41	ADAP 41 DELISTED Adaptimmune Therapeutics ADAP	49	-10	-17%	$103M
42	42 Fortress Biotech FBIO $64.7M	49	0	0%	$9.31M
43	ISEE 43 DELISTED IVERIC bio, Inc. Common Stock ISEE	48	-4	-8%	$17.3M
44	SIOX 44 DELISTED Sio Gene Therapies Inc. Common Stock SIOX	48	+9	+23%	$21.8M
45	45 Autolus Therapeutics AUTL $458M	43	-3	-7%	$167M
46	LOGC 46 DELISTED LogicBio Therapeutics, Inc. Common Stock LOGC	40	+3	+8%	$138M
47	TCRR 47 DELISTED TCR2 Therapeutics Inc. Common Stock TCRR	40	+7	+21%	$152M
48	48 DELISTED BRAINSTORM CELL THERAPUTC BCLI	39	+2	+5%	$8.24M
49	49 DELISTED Carisma Therapeutics CARM	37	-6	-14%	$27.3M
50	50 Neurogene NGNE $482M	36	+3	+9%	$53.7M