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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	BLCM 26 DELISTED Bellicum Pharmaceuticals, Inc. BLCM	79	-15	-16%	$42M
27	27 Krystal Biotech KRYS $9.79B	76	+19	+33%	$397M
28	PTE 28 DELISTED PolarityTE, Inc. Common Stock PTE	74	+3	+4%	$61.2M
29	29 Solid Biosciences SLDB $585M	74	0	0%	$128M
30	30 DELISTED BioLife Solutions BLFS	73	+7	+11%	$150M
31	31 Cellectis CLLS $113M	70	+7	+11%	$210M
32	32 Marker Therapeutics MRKR $14.8M	70	+14	+25%	$134M
33	RUBY 33 DELISTED Rubius Therapeutics, Inc RUBY	69	+2	+3%	$1.23B
34	34 MeiraGTx Holdings MGTX $904M	68	+13	+24%	$335M
35	ORTX 35 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	68	+25	+58%	$848M
36	36 Precision BioSciences DTIL $166M	63	+13	+26%	$291M
37	37 BridgeBio Pharma BBIO $12.7B	61	+61	–	$2.7B
38	ADAP 38 DELISTED Adaptimmune Therapeutics ADAP	59	-9	-13%	$274M
39	39 Mustang Bio MBIO $2.8M	55	+18	+49%	$40.1M
40	ISEE 40 DELISTED IVERIC bio, Inc. Common Stock ISEE	52	-6	-10%	$21.2M
41	41 Fortress Biotech FBIO $63.4M	49	0	0%	$9.37M
42	42 Adicet Bio ACET $45.8M	48	-1	-2%	$190M
43	AGTC 43 DELISTED Applied Genetic Technologies Corporation AGTC	46	-4	-8%	$25.9M
44	44 Autolus Therapeutics AUTL $450M	46	+11	+31%	$344M
45	45 Cartesian Therapeutics RNAC $192M	44	-12	-21%	$37.3M
46	46 DELISTED Carisma Therapeutics CARM	43	-5	-10%	$43.6M
47	SIOX 47 DELISTED Sio Gene Therapies Inc. Common Stock SIOX	39	-19	-33%	$19.1M
48	48 DELISTED BRAINSTORM CELL THERAPUTC BCLI	37	-1	-3%	$7.61M
49	LOGC 49 DELISTED LogicBio Therapeutics, Inc. Common Stock LOGC	37	+4	+12%	$165M
50	50 Neurogene NGNE $444M	33	-1	-3%	$39.3M