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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	ATNX 26 DELISTED Athenex, Inc. Common Stock ATNX	76	+5	+7%	$257M
27	27 Solid Biosciences SLDB $586M	74	-1	-1%	$157M
28	PTE 28 DELISTED PolarityTE, Inc. Common Stock PTE	71	-7	-9%	$110M
29	ADAP 29 DELISTED Adaptimmune Therapeutics ADAP	68	-12	-15%	$299M
30	RUBY 30 DELISTED Rubius Therapeutics, Inc RUBY	67	+10	+18%	$1.37B
31	31 DELISTED BioLife Solutions BLFS	66	+12	+22%	$154M
32	32 Cellectis CLLS $113M	63	-2	-3%	$234M
33	ISEE 33 DELISTED IVERIC bio, Inc. Common Stock ISEE	58	-5	-8%	$23.7M
34	SIOX 34 DELISTED Sio Gene Therapies Inc. Common Stock SIOX	58	-3	-5%	$49.7M
35	35 Krystal Biotech KRYS $9.79B	57	+12	+27%	$223M
36	36 Marker Therapeutics MRKR $14.8M	56	+13	+30%	$101M
37	37 Cartesian Therapeutics RNAC $192M	56	+2	+4%	$52.6M
38	38 MeiraGTx Holdings MGTX $904M	55	+17	+45%	$205M
39	AGTC 39 DELISTED Applied Genetic Technologies Corporation AGTC	50	-4	-7%	$30.8M
40	40 Precision BioSciences DTIL $166M	50	+50	–	$357M
41	41 Adicet Bio ACET $45.8M	49	+8	+20%	$128M
42	42 Fortress Biotech FBIO $63.4M	49	-12	-20%	$11.9M
43	43 DELISTED Carisma Therapeutics CARM	48	0	0%	$19.3M
44	ORTX 44 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	43	+6	+16%	$875M
45	45 DELISTED BRAINSTORM CELL THERAPUTC BCLI	38	+2	+6%	$10.5M
46	46 Mustang Bio MBIO $2.8M	37	+2	+6%	$8.31M
47	47 Autolus Therapeutics AUTL $450M	35	-3	-8%	$569M
48	48 Neurogene NGNE $444M	34	-2	-6%	$45.5M
49	LOGC 49 DELISTED LogicBio Therapeutics, Inc. Common Stock LOGC	33	-3	-8%	$124M
50	50 Pluri PLUR $11.7M	33	+1	+3%	$8.46M