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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	26 Allogene Therapeutics ALLO $449M	79	+79	–	$1.68B
27	PTE 27 DELISTED PolarityTE, Inc. Common Stock PTE	78	+9	+13%	$160M
28	28 Solid Biosciences SLDB $585M	75	-1	-1%	$648M
29	ATNX 29 DELISTED Athenex, Inc. Common Stock ATNX	71	-3	-4%	$238M
30	30 Cellectis CLLS $113M	65	-16	-20%	$191M
31	ISEE 31 DELISTED IVERIC bio, Inc. Common Stock ISEE	63	-5	-7%	$22.6M
32	32 Fortress Biotech FBIO $63.4M	61	-4	-6%	$6.44M
33	SIOX 33 DELISTED Sio Gene Therapies Inc. Common Stock SIOX	61	0	0%	$30M
34	RUBY 34 DELISTED Rubius Therapeutics, Inc RUBY	57	+2	+4%	$1.11B
35	AGTC 35 DELISTED Applied Genetic Technologies Corporation AGTC	54	-7	-11%	$19.5M
36	36 DELISTED BioLife Solutions BLFS	54	0	0%	$90.5M
37	37 Cartesian Therapeutics RNAC $192M	54	-11	-17%	$28M
38	38 DELISTED Carisma Therapeutics CARM	48	+1	+2%	$43.3M
39	39 Krystal Biotech KRYS $9.79B	45	+22	+96%	$129M
40	40 Marker Therapeutics MRKR $14.8M	43	+12	+39%	$86.4M
41	41 Adicet Bio ACET $45.8M	41	+1	+3%	$101M
42	42 Autolus Therapeutics AUTL $450M	38	-1	-3%	$558M
43	43 MeiraGTx Holdings MGTX $904M	38	+2	+6%	$69.6M
44	ORTX 44 DELISTED Orchard Therapeutics plc American Depositary Shares ORTX	37	+37	–	$765M
45	45 DELISTED BRAINSTORM CELL THERAPUTC BCLI	36	-1	-3%	$8.69M
46	LOGC 46 DELISTED LogicBio Therapeutics, Inc. Common Stock LOGC	36	+36	–	$131M
47	47 Neurogene NGNE $444M	36	-9	-20%	$38.3M
48	48 Mustang Bio MBIO $2.8M	35	-1	-3%	$7.25M
49	ONCS 49 DELISTED OncoSec Medical Incorporated ONCS	33	+1	+3%	$2.64M
50	50 Pluri PLUR $11.7M	32	-5	-14%	$4.96M