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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	26 Cellectis CLLS $113M	81	-5	-6%	$325M
27	27 Solid Biosciences SLDB $585M	76	+12	+19%	$878M
28	ATNX 28 DELISTED Athenex, Inc. Common Stock ATNX	74	+7	+10%	$262M
29	PTE 29 DELISTED PolarityTE, Inc. Common Stock PTE	69	-4	-5%	$217M
30	ISEE 30 DELISTED IVERIC bio, Inc. Common Stock ISEE	68	-5	-7%	$44.9M
31	31 Fortress Biotech FBIO $63.4M	65	0	0%	$13.7M
32	32 Cartesian Therapeutics RNAC $192M	65	+8	+14%	$178M
33	AGTC 33 DELISTED Applied Genetic Technologies Corporation AGTC	61	-3	-5%	$59M
34	SIOX 34 DELISTED Sio Gene Therapies Inc. Common Stock SIOX	61	-10	-14%	$22.8M
35	RUBY 35 DELISTED Rubius Therapeutics, Inc RUBY	55	+55	–	$1.54B
36	36 DELISTED BioLife Solutions BLFS	54	+5	+10%	$133M
37	37 DELISTED Carisma Therapeutics CARM	47	+1	+2%	$80.2M
38	38 Neurogene NGNE $444M	45	+1	+2%	$53.5M
39	39 Adicet Bio ACET $45.8M	40	-5	-11%	$177M
40	40 Autolus Therapeutics AUTL $450M	39	-9	-19%	$546M
41	41 DELISTED BRAINSTORM CELL THERAPUTC BCLI	37	-2	-5%	$9.04M
42	42 Pluri PLUR $11.7M	37	+2	+6%	$7.65M
43	43 Mustang Bio MBIO $2.8M	36	0	0%	$15.8M
44	44 MeiraGTx Holdings MGTX $904M	36	+13	+57%	$87.2M
45	ONCS 45 DELISTED OncoSec Medical Incorporated ONCS	32	-2	-6%	$10.4M
46	46 Marker Therapeutics MRKR $14.8M	31	+4	+15%	$11.9M
47	47 Ocugen OCGN $285M	30	+1	+3%	$5.65M
48	48 Opus Genetics IRD $341M	27	0	0%	$3.19M
49	49 Krystal Biotech KRYS $9.79B	23	+6	+35%	$47.6M
50	50 Mesoblast MESO $1.79B	23	+1	+5%	$23M