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Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	26 Rocket Pharmaceuticals RCKT $243M	76	+20	+36%	$664M
27	ISEE 27 DELISTED IVERIC bio, Inc. Common Stock ISEE	73	+2	+3%	$55.6M
28	PTE 28 DELISTED PolarityTE, Inc. Common Stock PTE	73	+38	+109%	$217M
29	SIOX 29 DELISTED Sio Gene Therapies Inc. Common Stock SIOX	71	-10	-12%	$25.8M
30	ATNX 30 DELISTED Athenex, Inc. Common Stock ATNX	67	+4	+6%	$245M
31	31 Fortress Biotech FBIO $63.4M	65	-1	-2%	$22.9M
32	AGTC 32 DELISTED Applied Genetic Technologies Corporation AGTC	64	+10	+19%	$32.6M
33	33 Solid Biosciences SLDB $586M	64	+6	+10%	$616M
34	34 Cartesian Therapeutics RNAC $192M	57	-2	-3%	$144M
35	35 DELISTED BioLife Solutions BLFS	49	+19	+63%	$51.9M
36	36 Autolus Therapeutics AUTL $450M	48	+48	–	$241M
37	37 DELISTED Carisma Therapeutics CARM	46	+19	+70%	$78.2M
38	38 Adicet Bio ACET $45.8M	45	+6	+15%	$108M
39	39 Neurogene NGNE $444M	44	-6	-12%	$46.2M
40	40 DELISTED BRAINSTORM CELL THERAPUTC BCLI	39	+5	+15%	$9.49M
41	41 Mustang Bio MBIO $2.8M	36	+15	+71%	$17.9M
42	42 Pluri PLUR $11.7M	35	0	0%	$4.89M
43	ONCS 43 DELISTED OncoSec Medical Incorporated ONCS	34	-4	-11%	$18.9M
44	44 Ocugen OCGN $285M	29	+1	+4%	$33.5M
45	45 Opus Genetics IRD $341M	27	+1	+4%	$2.58M
46	46 Marker Therapeutics MRKR $14.8M	27	+16	+145%	$14.1M
47	47 MeiraGTx Holdings MGTX $904M	23	+23	–	$74.6M
48	48 Mesoblast MESO $1.79B	22	-7	-24%	$14.3M
49	49 Capricor Therapeutics CAPR $383M	19	-1	-5%	$3.25M
50	50 Imunon IMNN $5.84M	19	-3	-14%	$2.52M