← All themes Genomics & Gene Editing

Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

#	Name	Funds holding	Growth	Growth %	Fund value
26	AGTC 26 DELISTED Applied Genetic Technologies Corporation AGTC	62	-5	-7%	$30M
27	27 Fortress Biotech FBIO $64M	62	+4	+7%	$24.4M
28	28 uniQure QURE $1.5B	62	+26	+72%	$267M
29	29 Cellectis CLLS $111M	57	+15	+36%	$213M
30	30 Neurogene NGNE $470M	52	+9	+21%	$253M
31	31 Vericel Corp VCEL $2.1B	50	+10	+25%	$73.4M
32	ATNX 32 DELISTED Athenex, Inc. Common Stock ATNX	45	+12	+36%	$59.1M
33	33 Pluri PLUR $12M	39	+6	+18%	$6.37M
34	34 DELISTED BRAINSTORM CELL THERAPUTC BCLI	35	+3	+9%	$7.11M
35	ONCS 35 DELISTED OncoSec Medical Incorporated ONCS	34	+14	+70%	$7.3M
36	36 Rocket Pharmaceuticals RCKT $251M	34	-1	-3%	$32.1M
37	37 DELISTED BioLife Solutions BLFS	31	+7	+29%	$10.3M
38	PTE 38 DELISTED PolarityTE, Inc. Common Stock PTE	30	+8	+36%	$18.8M
39	39 Opus Genetics IRD $350M	28	+7	+33%	$3.28M
40	40 Ocugen OCGN $276M	25	+5	+25%	$25.2M
41	41 DELISTED Carisma Therapeutics CARM	23	+1	+5%	$5.39M
42	42 Capricor Therapeutics CAPR $400M	22	+3	+16%	$3.84M
43	43 Imunon IMNN $5.89M	20	+9	+82%	$1.82M
44	44 Mesoblast MESO $1.78B	20	+2	+11%	$15.8M
45	45 Krystal Biotech KRYS $9.99B	13	0	0%	$34M
46	46 Mustang Bio MBIO $2.87M	11	+10	+1,000%	$9.18M
47	CYAD 47 DELISTED Celyad Oncology SA American Depositary Shares CYAD	10	+5	+100%	$20.4M
48	48 Eterna Therapeutics ERNA $2.47M	9	+1	+13%	$3.31M
49	49 Marker Therapeutics MRKR $15.9M	8	0	0%	$904K
50	50 Benitec Biopharma BNTC $299M	6	+3	+100%	$190K