← All themes Genomics & Gene Editing

Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

# Name Holding Trade Value Theme
Stocks
% of
Portfolio
Status
76
HA
HHLR Advisors
Cayman Islands
$203M -$29.6M 2 5.74% Reduced
77
Citigroup
Citigroup
New York
$203M +$42.2M 64 0.1% Increased
78
SOCM
SR One Capital Management
Pennsylvania
$199M $0 4 51.15% Maintained
79
ClearBridge Investments
ClearBridge Investments
New York
$195M -$26.8M 4 0.17% Reduced
80
Capital Research Global Investors
Capital Research Global Investors
California
$191M -$14.6M 2 0.04% Reduced
81
B
Braidwell
Connecticut
$188M -$25.7M 3 6.62% Reduced
82
BBA
Baker Bros. Advisors
New York
$186M -$37.1M 15 2.06% Reduced
83
SEI Investments
SEI Investments
Pennsylvania
$184M +$4.28M 30 0.24% Increased
84
IC
Impactive Capital
New York
$182M +$1.54M 1 8.34% Increased
85
Woodline Partners
Woodline Partners
California
$177M -$27M 26 1.15% Reduced
86
Ariel Investments
Ariel Investments
Illinois
$166M +$5.61M 1 1.95% Increased
87
Toronto Dominion Bank
Toronto Dominion Bank
Ontario, Canada
$164M -$12.9M 10 0.32% Reduced
88
CAM
Cormorant Asset Management
Massachusetts
$162M +$10.2M 4 12.2% Increased
89
Driehaus Capital Management
Driehaus Capital Management
Illinois
$160M +$55.7M 4 1.54% Increased
90
Arrowstreet Capital
Arrowstreet Capital
Massachusetts
$155M +$154M 2 0.13% Increased
91
Mackenzie Financial
Mackenzie Financial
Ontario, Canada
$155M +$4.14M 9 0.22% Increased
92
Two Sigma Advisers
Two Sigma Advisers
New York
$154M +$66.9M 32 0.35% Increased
93
Sands Capital Management
Sands Capital Management
Virginia
$151M -$5.59M 1 0.51% Reduced
94
Manulife (Manufacturers Life Insurance)
Manulife (Manufacturers Life Insurance)
Ontario, Canada
$150M -$434K 37 0.14% Reduced
95
Balyasny Asset Management
Balyasny Asset Management
Illinois
$149M +$14.5M 19 0.25% Increased
96
Scharf Investments
Scharf Investments
California
$140M +$5.89M 1 4.24% Increased
97
Susquehanna International Group
Susquehanna International Group
Pennsylvania
$135M -$26.5M 75 0.02% Reduced
98
BCM
Brown Capital Management
Maryland
$129M -$19.1M 2 3.88% Reduced
99
CCM
Camber Capital Management
Massachusetts
$127M -$106M 2 4.53% Reduced
100
Chevy Chase Trust
Chevy Chase Trust
Maryland
$127M -$9.71M 3 0.41% Reduced