← All themes Genomics & Gene Editing

Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

# Name Holding Trade Value Theme
Stocks
% of
Portfolio
Status
26
Loomis, Sayles & Company
Loomis, Sayles & Company
Massachusetts
$736M -$344K 3 1.01% Reduced
27
ARK Investment Management
ARK Investment Management
Florida
$712M -$6.66M 4 6.31% Reduced
28
RA Capital Management
RA Capital Management
Massachusetts
$711M +$124M 11 9.4% Increased
29
T. Rowe Price Investment Management
T. Rowe Price Investment Management
Maryland
$700M -$235M 10 0.44% Reduced
30
Viking Global Investors
Viking Global Investors
Connecticut
$698M $0 2 2.68% Maintained
31
Nomura Holdings
Nomura Holdings
Japan
$637M -$11.7M 6 1.22% Reduced
32
Norges Bank
Norges Bank
Norway
$630M +$23.8M 18 0.09% Increased
33
Citadel Advisors
Citadel Advisors
Florida
$626M +$4.66M 64 0.13% Increased
34
EC
EcoR1 Capital
California
$625M -$47.8M 13 19.11% Reduced
35
Millennium Management
Millennium Management
New York
$610M +$110M 64 0.28% Increased
36
Charles Schwab
Charles Schwab
California
$580M +$44.4M 57 0.11% Increased
37
Deutsche Bank
Deutsche Bank
Germany
$557M +$98M 51 0.25% Increased
38
Perceptive Advisors
Perceptive Advisors
New York
$538M -$79.7M 13 12.96% Reduced
39
CC
Casdin Capital
New York
$485M +$16.3M 10 37.02% Increased
40
Paradigm Biocapital Advisors
Paradigm Biocapital Advisors
New York
$485M -$68.4M 6 18.55% Reduced
41
Capital World Investors
Capital World Investors
California
$483M -$429M 4 0.08% Reduced
42
Adage Capital Partners
Adage Capital Partners
Massachusetts
$470M +$39M 24 0.87% Increased
43
Barclays
Barclays
United Kingdom
$431M +$9.69M 65 0.13% Increased
44
Principal Financial Group
Principal Financial Group
Iowa
$425M +$21.8M 30 0.25% Increased
45
ClearBridge Investments
ClearBridge Investments
New York
$417M -$23.7M 4 0.34% Reduced
46
Renaissance Technologies
Renaissance Technologies
New York
$410M -$40.4M 57 0.7% Reduced
47
UBS Group
UBS Group
Switzerland
$407M -$19.6M 88 0.1% Reduced
48
Balyasny Asset Management
Balyasny Asset Management
Illinois
$397M +$209M 21 0.69% Increased
49
RG
Redmile Group
California
$397M -$84.3M 11 24% Reduced
50
Wells Fargo
Wells Fargo
California
$396M +$12.5M 75 0.1% Increased