RGNX icon

Regenxbio

9.02 USD
-0.24
2.59%
At close Updated Sep 17, 4:00 PM EDT
Pre-market
After hours
9.03
+0.01
0.11%
1 day
-2.59%
5 days
-5.85%
1 month
3.56%
3 months
4.16%
6 months
28.86%
Year to date
14.76%
1 year
-30.35%
5 years
-69.44%
10 years
-70.38%
 

About: Regenxbio Inc is a biotechnology company. Its main activity is the development and commercialization of recombinant adeno associated virus gene therapy to correct an underlying genetic defect. The diseases that the Regenxbio platform targets are metabolic (homozygous familial hypercholesterolemia), neurodegenerative conditions (mucopolysaccharidosis), and retinal diseases (wet age-related macular degeneration, X-linked retinitis pigmentosa). The company derives the majority of its revenue from the United States.

Employees: 353

0
Funds holding %
of 7,463 funds
0
Analysts bullish %
of 4 analysts

Fund manager confidence

Based on 2025 Q2 regulatory disclosures by fund managers ($100M+ AUM)

21% more call options, than puts

Call options by funds: $1.17M | Put options by funds: $972K

20% more repeat investments, than reductions

Existing positions increased: 60 | Existing positions reduced: 50

16% more capital invested

Capital invested by funds: $298M [Q1] → $345M (+$47.2M) [Q2]

0.24% more ownership

Funds ownership: 83.18% [Q1] → 83.42% (+0.24%) [Q2]

3% less funds holding

Funds holding: 164 [Q1] → 159 (-5) [Q2]

11% less first-time investments, than exits

New positions opened: 25 | Existing positions closed: 28

67% less funds holding in top 10

Funds holding in top 10: 3 [Q1] → 1 (-2) [Q2]

Research analyst outlook

4 Wall Street Analysts provided 1 year price targets over the past 3 months

Low target
$17
88% upside
Avg. target
$35
288% upside
High target
$52
476% upside

4 analyst ratings

positive
100%
neutral
0%
negative
0%
HC Wainwright & Co.
Yi Chen
$34
Buy
Reiterated
8 Sep 2025
Chardan Capital
Daniil Gataulin
$52
Buy
Maintained
8 Sep 2025
RBC Capital
Luca Issi
$17
Outperform
Maintained
8 Aug 2025
Barclays
Gena Wang
$37
Overweight
Maintained
8 Aug 2025

Financial journalist opinion

Based on 7 articles about RGNX published over the past 30 days

Positive
Seeking Alpha
8 days ago
Regenxbio: Poised For Breakthrough With RGX-121 Gene Therapy In Hunter Syndrome
Regenxbio's RGX-121 gene therapy for Hunter syndrome is the main catalyst, with FDA approval targeted for February 2026. Recent clinical data shows RGX-121 can address neurological decline, a major unmet need, setting it apart from current treatments. Despite a small patient population, premium pricing and first-mover advantage could drive substantial revenue if RGX-121 is approved.
Regenxbio: Poised For Breakthrough With RGX-121 Gene Therapy In Hunter Syndrome
Neutral
Seeking Alpha
9 days ago
REGENXBIO Inc. (RGNX) Presents At Morgan Stanley 23rd Annual Global Healthcare Conference Transcript
REGENXBIO Inc. (NASDAQ:RGNX ) Morgan Stanley 23rd Annual Global Healthcare Conference September 8, 2025 11:30 AM EDT Company Participants Curran Simpson - President, CEO & Director Steve Pakola - Executive VP & Chief Medical Officer Mitchell Chan - Executive VP & CFO Presentation Unknown Analyst Welcome, everyone, to this session of the Morgan Stanley Global Healthcare Conference. We're excited to have team from REGENX here.
REGENXBIO Inc. (RGNX) Presents At Morgan Stanley 23rd Annual Global Healthcare Conference Transcript
Positive
Seeking Alpha
11 days ago
Regenxbio: Remains A "Buy Rating" Despite BLA Review Delay Of RGX-121 For Hunter Syndrome
Regenxbio's RGX-121 for Hunter syndrome saw its FDA review delayed to February 8, 2026, but strong 12-month surrogate endpoint data supports its potential as a gene therapy. Late-stage Sura-vec trials for Wet-AMD, in partnership with AbbVie, remain on track for 2026 topline results, bolstering the pipeline's value. Recent partnerships and royalty deals have strengthened Regenxbio's cash position, extending its runway into early 2027 despite ongoing R&D expenses.
Regenxbio: Remains A "Buy Rating" Despite BLA Review Delay Of RGX-121 For Hunter Syndrome
Neutral
PRNewsWire
12 days ago
REGENXBIO Presents Positive Twelve-Month Pivotal Data from Phase I/II/III CAMPSIITE® Trial of RGX-121 for Treatment of MPS II
12-month pivotal data further demonstrate the ability of one-time RGX-121 treatment to improve outcomes for patients with MPS II >80% reduction in CSF levels of HS D2S6, key biomarker of MPS II brain disease, sustained through 1 year Pivotal patients demonstrate continued skill acquisition or stability, stratified by baseline function, through 1 year Primary endpoint of CSF HS D2S6 reduction at week 16 met; strong correlation to neurodevelopmental outcomes at 1 year, supporting HS D2S6 as surrogate biomarker reasonably likely to predict clinical benefit RGX-121 would be the first and only potential one-time, commercially-available therapy designed to directly address the underlying genetic cause of Hunter syndrome, if approved ROCKVILLE, Md. , Sept. 5, 2025 /PRNewswire/ -- REGENXBIO Inc. (Nasdaq: RGNX) today announced new, positive data from the Phase I/II/III CAMPSIITE® trial of clemidsogene lanparvovec (RGX-121) for the treatment of patients with Mucopolysaccharidosis Type II (MPS II), also known as Hunter syndrome, at the International Congress of Inborn Errors of Metabolism (ICIEM) 2025.
REGENXBIO Presents Positive Twelve-Month Pivotal Data from Phase I/II/III CAMPSIITE® Trial of RGX-121 for Treatment of MPS II
Neutral
PRNewsWire
20 days ago
REGENXBIO to Participate in Upcoming Investor Conferences
ROCKVILLE, Md. , Aug. 28, 2025 /PRNewswire/ -- REGENXBIO Inc. (Nasdaq: RGNX) today announced it will participate in the following investor conferences: 2025 Wells Fargo Healthcare Conference 1x1 Investor Meetings: Thursday, September 4 Location:  Boston, MA Morgan Stanley 23rd Annual Global Healthcare Conference Fireside Chat:  Monday, September 8, 2025 at 11:30 a.m.
REGENXBIO to Participate in Upcoming Investor Conferences
Negative
Benzinga
29 days ago
FDA Extends Decision Date On Regenxbio's Gene Therapy Into Next Year
The U.S. Food and Drug Administration (FDA) on Monday extended its review timeline for REGENXBIO Inc.'s RGNX Biologics License Application (BLA) for clemidsogene lanparvovec (RGX-121) for Mucopolysaccharidosis II (MPS II), also known as Hunter syndrome.
FDA Extends Decision Date On Regenxbio's Gene Therapy Into Next Year
Neutral
PRNewsWire
29 days ago
REGENXBIO Announces FDA Review Extension of BLA for RGX-121 to Treat Patients with MPS II
RGX-121 would be the first and only potential one-time commercially-available therapy designed to directly address the underlying genetic cause of Hunter syndrome, if approved Commercial launch plans remain on track  REGENXBIO plans to present updated pivotal data during the ICIEM meeting in September 2025 ROCKVILLE, Md. , Aug. 18, 2025 /PRNewswire/ -- REGENXBIO Inc. (Nasdaq: RGNX) today announced that the U.S. Food and Drug Administration (FDA) extended its review timeline of the Biologics License Application (BLA) for clemidsogene lanparvovec (RGX-121) for the treatment of Mucopolysaccharidosis II (MPS II), also known as Hunter syndrome.
REGENXBIO Announces FDA Review Extension of BLA for RGX-121 to Treat Patients with MPS II
Neutral
Seeking Alpha
1 month ago
REGENXBIO Inc. (RGNX) Q2 2025 Earnings Call Transcript
REGENXBIO Inc. (NASDAQ:RGNX ) Q2 2025 Earnings Call August 7, 2025 8:00 AM ET Company Participants Curran M. Simpson - President, CEO & Director Mitchell Chan - Executive VP & CFO Patrick J.
REGENXBIO Inc. (RGNX) Q2 2025 Earnings Call Transcript
Negative
Zacks Investment Research
1 month ago
Regenxbio (RGNX) Reports Q2 Loss, Lags Revenue Estimates
Regenxbio (RGNX) came out with a quarterly loss of $1.38 per share versus the Zacks Consensus Estimate of a loss of $1.13. This compares to a loss of $1.05 per share a year ago.
Regenxbio (RGNX) Reports Q2 Loss, Lags Revenue Estimates
Neutral
PRNewsWire
1 month ago
REGENXBIO Reports Second Quarter 2025 Financial Results and Operational Highlights
RGX-202 in Duchenne muscular dystrophy on track for topline results 1H 2026 and BLA submission mid-2026 Pivotal trial enrollment accelerated, expected to complete in October 2025 ahead of previous guidance Clemidsogene lanparvovec (RGX-121) on track to be first gene therapy and one-time treatment for MPS II; FDA inspections completed successfully Pre-license inspection (PLI) of in-house manufacturing facility, quality systems and processes completed with no observations Bioresearch monitoring information (BIMO) inspection of laboratory and clinical data practices completed with no observations Surabgene lomparvovec (sura-vec, ABBV-RGX-314) on track to be first gene therapy in chronic retinal disease Pivotal data evaluating the safety and efficacy of the subretinal delivery of sura-vec in patients with wet AMD are expected in 2026 Sura-vec using suprachoroidal delivery for diabetic retinopathy advancing to global pivotal program, supported by positive Phase II trial data Conference call today at 8:00 a.m. ET ROCKVILLE, Md.
REGENXBIO Reports Second Quarter 2025 Financial Results and Operational Highlights
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