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Genomics & Gene Editing

Genomics reads the genetic code and gene editing rewrites it, which can turn an inherited disease from a lifelong condition into a single treatment. Sequencing cost has fallen far enough to make study at population scale routine.

199 stocks

Name Funds
holding
Growth Growth % Fund
value
ORTX
151
DELISTED
Orchard Therapeutics plc American Depositary Shares
ORTX
– – – –
PASG icon
152
Passage Bio
PASG
$11.3M
– – – –
PEPG icon
153
PepGen
PEPG
$180M
– – – –
PMCB icon
154
PharmaCyte Biotech
PMCB
$3.65M
– – – –
PRME icon
155
Prime Medicine
PRME
$629M
– – – –
PROK icon
156
ProKidney
PROK
$278M
– – – –
PRQR icon
157
ProQR Therapeutics
PRQR
$185M
– – – –
PSNL icon
158
Personalis
PSNL
$1.67B
– – – –
PSTX icon
159
DELISTED
Poseida Therapeutics, Inc. Common Stock
PSTX
– – – –
PTE
160
DELISTED
PolarityTE, Inc. Common Stock
PTE
– – – –
QGEN icon
161
Qiagen
QGEN
$9.53B
– – – –
QSI icon
162
Quantum-Si Incorporated
QSI
$245M
– – – –
QURE icon
163
uniQure
QURE
$1.51B
– – – –
RARE icon
164
Ultragenyx Pharmaceutical
RARE
$1.43B
– – – –
RCKT icon
165
Rocket Pharmaceuticals
RCKT
$239M
– – – –
RCOR
166
DELISTED
Renovacor, Inc.
RCOR
– – – –
RGNX icon
167
Regenxbio
RGNX
$457M
– – – –
RNA icon
168
Atrium Therapeutics
RNA
$131M
– – – –
RNAC icon
169
Cartesian Therapeutics
RNAC
$190M
– – – –
RUBY
170
DELISTED
Rubius Therapeutics, Inc
RUBY
– – – –
SANA icon
171
Sana Biotechnology
SANA
$680M
– – – –
SCPS
172
DELISTED
Scopus BioPharma Inc. Common Stock
SCPS
– – – –
SCTX
173
Scribe Therapeutics Inc
SCTX
$380M
– – – –
SGTX
174
DELISTED
Sigilon Therapeutics, Inc. Common Stock
SGTX
– – – –
SIOX
175
DELISTED
Sio Gene Therapies Inc. Common Stock
SIOX
– – – –