← All themes Genomics & Gene Editing

Gene Therapy

Gene therapy delivers a working copy of a gene, or a correction to a faulty one, usually once and for life. Manufacturing the delivery vector is often harder than designing the therapy.

131 stocks

# Name Holding Trade Value Theme
Stocks
% of
Portfolio
Status
126
RSCM
Rock Springs Capital Management
Maryland
$84.3M +$6.9M 7 3.98% Increased
127
Susquehanna International Group
Susquehanna International Group
Pennsylvania
$80M -$27.7M 26 0.03% Reduced
128
Westfield Capital Management
Westfield Capital Management
Massachusetts
$79.4M +$30.9M 4 0.68% Increased
129
CAM
Cormorant Asset Management
Massachusetts
$78.7M -$13.7M 9 6.39% Reduced
130
Marshall Wace North America
Marshall Wace North America
New York
$77M +$1.34M 15 0.74% Increased
131
Scharf Investments
Scharf Investments
California
$76.8M +$7.56M 1 3.05% Increased
132
Nantahala Capital Management
Nantahala Capital Management
Connecticut
$76.1M +$21M 2 2.34% Increased
133
Cullen Capital Management
Cullen Capital Management
New York
$74.2M -$2.22M 1 3.2% Reduced
134
Madison Investment Holdings
Madison Investment Holdings
Wisconsin
$74M -$1.99M 1 1.49% Reduced
135
Wasatch Advisors
Wasatch Advisors
Utah
$73.5M +$18.1M 4 0.98% Increased
136
WM
WS Management
Florida
$72.8M -$3.85M 13 3.54% Reduced
137
Citigroup
Citigroup
New York
$72M +$23.3M 41 0.07% Increased
138
Eaton Vance Management
Eaton Vance Management
Massachusetts
$71.6M +$25.6M 6 0.19% Increased
139
PHS
PFM Health Sciences
California
$71.3M +$6.23M 3 1.89% Increased
140
Armistice Capital
Armistice Capital
New York
$68.8M +$34M 6 5.22% Increased
141
AVM
Arch Venture Management
Illinois
$68.7M +$76.6M 2 68.68% New
142
John W. Bristol & Co
John W. Bristol & Co
New York
$68.4M -$4.11M 1 2.15% Reduced
143
Van Berkom & Associates
Van Berkom & Associates
Quebec, Canada
$66.1M -$2.53M 1 2.33% Reduced
144
Two Sigma Investments
Two Sigma Investments
New York
$66.1M +$1.73M 24 0.26% Increased
145
6CM
683 Capital Management
New York
$66.1M +$27.8M 9 4% Increased
146
EC
EcoR1 Capital
California
$63.9M +$15.6M 6 6.39% Increased
147
Erste Asset Management
Erste Asset Management
Austria
$63.1M +$74.2M 6 4.24% New
148
Capital Guardian Trust
Capital Guardian Trust
California
$62.7M +$1.26M 3 1% Increased
149
Swiss National Bank
Swiss National Bank
Switzerland
$61M +$4.78M 22 0.08% Increased
150
TGI
TRV GP III
Massachusetts
$60.1M $0 1 50.34% Maintained